Diseases Treated with Stem Cells

 

Bone Marrow Failure Disorders

* Amegakaryocytosis
* Aplastic Anemia (Severe)
* Blackfan-Diamond Anemia
* Congenital Cytopenia
* Congenital Dyserythropoietic Anemia
* Dyskeratosis Congenita
* Fanconi Anemia
* Paroxysmal Nocturnal Hemoglobinuria (PNH)
* Pure Red Cell Aplasia

Hemoblobinopathies

* Beta Thalassemia Major
* Sickle Cell Disease

Histiocytic Disorders

* Familial Erythrophagocytic Lymphohistiocytosis
* Hemophagocytosis
* Langerhans' Cell Histiocytosis (Histiocytosis X)

Inherited Immune System Disorders

* Chronic Granulomatous Disease
* Congenital Neutropenia
* Leukocyte Adhesion Deficiency
* Severe Combined Immunodeficiencies (SCID) including:

o Adenosine Deaminase Deficiency
o Bare Lymphocyte Syndrome
o Chediak-Higashi Syndrome
o Kostmann Syndrome
o Omenn Syndrome
o Purine Nucleoside Phosphorylase Deficiency
o Reticular Dysgenesis

* Wiskott-Aldrich Syndrome
* X-Linked Lymphoproliferative Disorder

Inherited Metabolic Disorders

* Adrenoleukodystrophy * Fucosidosis
* Gaucher Disease
* Hunter Syndrome (MPS-II)
* Hurler Syndrome (MPS-IH)
* Krabbe Disease
* Lesch-Nyhan Syndrome
* Mannosidosis
* Maroteaux-Lamy Syndrome (MPS-VI)
* Metachromatic Leukodystrophy
* Mucolipidosis II (I-cell Disease)
* Neuronal Ceroid Lipofuscinosis (Batten Disease)
* Niemann-Pick Disease
* Sandhoff Disease
* Sanfilippo Syndrome (MPS-III)
* Scheie Syndrome (MPS-IS)
* Sly Syndrome
* Tay Sachs
* Wolman Disease

Leukemias and Lymphomas

* Acute Biphenotypic Leukemia
* Acute Lymphocytic Leukemia (ALL)
* Acute Myelogenous Leukemia (AML)
* Acute Undifferentiated Leukemia
* Adult T Cell Leukemia/Lymphoma
* Chronic Lymphocytic Leukemia (CLL)
* Chronic Myelogenous Leukemia (CML)
* Hodgkin's Lymphoma
* Juvenile Chronic Myelogenous Leukemia (JCML)
* Juvenile Myelomonocytic Leukemia (JMML)
* Myeloid/Natural Killer (NK) Cell Precursor Acute Leukemia
* Non-Hodgkin's Lymphoma
* Polymphocytic Leukemia

Myelodysplastic/Myeloproliferative Disorders

* Acute Myelofibrosis
* Agnogenic Myeloid Metaplasia (Myelofibrosis)
* Amyloidosis
* Chronic Myelomonocytic Leukemia (CMML)
* Essential Thrombocythemia
* Polycythemia Vera
* Refractory Anemias (RA) including:
o Refractory Anemia with Excess Blasts (RAEB)
o Refractory Anemia with Excess Blasts in Transformation (RAEB-T)
o Refractory Anemia with Ringed Sideroblasts (RARS)

Plasma Cell Disorders

* Multiple Myeloma
* Plasma Cell Leukemia
* Waldenstrom's Macroglobulinemia

Other Inherited Disorders

* Cartilage-Hair Hypoplasia
* Congenital Erythropoietic Porphyria (Gunther Disease)
* DiGeorge Syndrome
* Osteopetrosis

Other Malignancies

* Brain Tumors
* Ewing Sarcoma
* Neuroblastoma
* Ovarian Cancer
* Renal Cell Carcinoma
* Rhabdomyosarcoma
* Small Cell Lung Cancer
* Testicular Cancer
* Thymoma (Thymic Carcinoma)

Other

* Chronic Active Epstein Barr
* Evans Syndrome
* Multiple Sclerosis
* Rheumatoid Arthritis
* Systemic Lupus Erythematosus
* Thymic Dysplasia

Emerging Stem Cell Applications

* Diabetes
* Heart Disease
* Liver Disease
* Muscular Dystrophy
* Parkinson's Disease
* Spinal Cord Injury * Stroke